All Industries

Top Drug Discovery Companies

234 Drug Discovery companies, sorted by total funding raised.

CHARM Therapeutics

AI-driven biotech developing next-generation menin inhibitors and small-molecule therapeutics for...

London, United Kingdom11–50Life Sciences, Biotech
Series B·$130.0M·Sep 2025
Monte Rosa TherapeuticsIPO

Monte Rosa Therapeutics is a biotechnology company developing molecular glues to degrade disease-...

Boston, United States51–200Biotech, Drug Discovery
Series C·$127.5M·Mar 2021
Gate Bioscience

Biotechnology company developing oral small-molecule ‘molecular gates’ to eliminate disease-causi...

California, United States11–50Biotech, Drug Discovery
Series B·$125.0M·Nov 2025
Alexza PharmaceuticalsIPO

Staccato

Mountain View, United States51–200Biotech, Drug Discovery
Series D·$124.5M·Jul 2012
Atomwise

Artificial intelligence for drug discovery.

San Francisco, United States51–200Biotech, Artificial Intelligence
Series B·$123.0M·Aug 2020
Ouro Medicines

Biotechnology company dedicated to developing immune reset therapeutics for people living with ch...

USA, United States11–50Biotech, Immunology
Series A·$120.0M·Jan 2025
BenevolentAI

AI-enabled drug discovery company using machine learning and knowledge graphs to identify novel d...

London, United Kingdom201–500Drug Discovery, Artificial Intelligence
Venture Unknown·$115.0M·Apr 2018
O
Octant

Therapeutics company pioneering small molecule drug discovery by engineering biology and chemistr...

South San Francisco, United States51–200Biotech, Drug Discovery
Grant·$114.9M·Jun 2025
Healx

AI-enabled biotech using generative AI to discover and develop treatments for rare diseases, adva...

Cambridge, United Kingdom51–200Artificial Intelligence, Biotech
Series C·$113.0M·Aug 2024
K36 Therapeutics

Clinical-stage biotech developing selective oral NSD2/MMSET inhibitors for multiple myeloma and p...

New York, United States1–10Biotech, Drug Discovery
Series B·$100.0M·Jun 2023
IconOVir Bio

Preclinical-stage biotech developing next-generation oncolytic virus therapies for solid tumors.

San Diego, United States11–50Biotech, Drug Discovery
Venture Unknown·$97.2M·Jun 2024
PillPackAcquired

PillPack is an online pharmacy that simplifies medication management by pre-sorting and deliverin...

Manchester, United States501–1000Drug Discovery, E-Commerce
Series D·$93.5M·Sep 2016
Orbis Medicines

Orbis Medicines is pioneering a new era for oral macrocycle drug discovery.

Copenhagen, Denmark11–50Biotech, Drug Discovery
Series B·$93.0M·Jan 2025
Xilis

Develops MicroOrganoSphere ex vivo tumor models and AI analytics to guide precision oncology and ...

Durham, United States51–200Biotech, Diagnostics
Series A·$92.0M·Apr 2025
Phil

Software therapy deployment platform simplifying prescription management, delivery, and patient a...

San Francisco, United States51–200Drug Discovery, Healthcare
Series D·$91.0M·Jun 2021
Nautilus BiotechnologyIPO

Accurate single-molecule quantification of proteins and proteoforms

Seattle, United States51–200Artificial Intelligence, Healthcare
Corporate Round·$90.7M·Jul 2021
Maxion Therapeutics

Biotech developing antibody-based KnotBody therapeutics targeting ion channels and GPCRs to treat...

Cambridge, United Kingdom11–50Life Sciences, Biotech
Series A·$88.0M·Mar 2025
Amicus TherapeuticsIPO

Oral pharmacological chaperone protein therapies to address diseases that result from protein mis...

Cranbury, United States501–1000Biotech, Drug Discovery
Venture Unknown·$86.0M·Jan 2006
Tempest TherapeuticsIPO

A clinical-stage oncology company advancing small molecules that combine both targeted and immune...

Brisbane, United States11–50Biotech, Drug Discovery
Private Equity·$85.0M·Apr 2022
Notable LabsIPO

Personalized drug discovery for blood cancer.

Foster City, United States11–50Biotech, Drug Discovery
Venture Unknown·$77.4M·Feb 2023
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Nimble Rx

Nimble RX is an online pharmacy that offers free same-day delivery.

Redwood City, United States51–200Drug Discovery, Healthcare
Venture Unknown·$74.8M·Jun 2022
Vilya

Computational biotechnology company designing de novo macrocycles with AI for therapeutic drug di...

Seattle, United States11–50Artificial Intelligence, Biotech
Series A·$71.0M·Jun 2024
Credence

Award-winning innovator in injectable drug delivery devices for pharmaceutical and biotechnology ...

Menlo Park, United States11–50Healthcare, Drug Discovery
Series D·$67.6M·Dec 2024
Surge Therapeutics

Develops an injectable intraoperative immunotherapy hydrogel to prevent post-surgical cancer recu...

Cambridge, United States1–10Biotech, Drug Discovery
Series B·$58.0M·Jul 2023
Moonwalk Biosciences

Develops precision epigenetic medicines targeting adipose biology and cardiometabolic disease usi...

South San Francisco, United States11–50Biotech, Drug Discovery
Seed·$57.0M·Jan 2024