Top Therapeutics Companies

Metacrine is a biotech company developing innovative therapeutics for liver, gastrointestinal, an...

Biotechnology company dedicated to developing immune reset therapeutics for people living with ch...

Develops immune-evasive iPSC-derived off-the-shelf cell therapies for cancer and autoimmune disea...

GenEdit is revolutionizing gene therapy and gene editing with its nanoparticle delivery technology.

Nkarta is a clinical-stage biotechnology company advancing the development of allogeneic natural ...

Biotech company focused on cell and gene therapy development.

Biotechnology company applying artificial intelligence to design novel AAV vectors for gene thera...

Digital therapeutics and behavioral health company using software as medicine.

Develops off-the-shelf liver cell therapies that deliver functional hepatocytes to restore liver ...

Biopharmaceutical company focused on drugs to treat CNS disorders by targeting neuronal nicotinic...

Private biopharmaceutical company focused on the development of therapies for retinal dystrophies.

Preclinical-stage biotech developing next-generation oncolytic virus therapies for solid tumors.

Orbis Medicines is pioneering a new era for oral macrocycle drug discovery.

Biotech developing antibody-based KnotBody therapeutics targeting ion channels and GPCRs to treat...

Oral pharmacological chaperone protein therapies to address diseases that result from protein mis...

A clinical-stage oncology company advancing small molecules that combine both targeted and immune...

A next-generation gene therapy company pioneering the development of targeted non-viral gene ther...

Clinical-stage biopharma developing topical nanoparticle therapies for eye diseases, including tr...

Develops and commercializes neffy, an FDA-approved needle-free epinephrine nasal spray for treati...

Clinical-stage biotech developing immunotherapies that reprogram immune signaling to treat cancer...

Clinical-stage gene editing company developing in vivo therapies using its proprietary ARCUS geno...

Spark Therapeutics develops gene therapy treatments for debilitating genetic diseases; acquired b...

Biotech developing 'activation lethality' cancer therapeutics that overactivate oncogenes to sele...

Develops microscale wireless micro-robots to deliver therapies and diagnostics to deep body locat...

Biotech company using click chemistry to selectively activate cancer drugs at the tumor site, imp...