Top Therapeutics Companies

Biotechnology company developing oral small-molecule ‘molecular gates’ to eliminate disease-causi...

Clinical-stage biopharma developing targeted oncology therapeutics and ADCs to advance treatments...

Epic Bio (now Epicrispr Biotechnologies) develops epigenetic gene therapies using ultracompact CR...

Metacrine is a biotech company developing innovative therapeutics for liver, gastrointestinal, an...

Biotechnology company dedicated to developing immune reset therapeutics for people living with ch...

Develops immune-evasive iPSC-derived off-the-shelf cell therapies for cancer and autoimmune disea...

GenEdit is revolutionizing gene therapy and gene editing with its nanoparticle delivery technology.

Nkarta is a clinical-stage biotechnology company advancing the development of allogeneic natural ...

Biotech company focused on cell and gene therapy development.

Biotechnology company applying artificial intelligence to design novel AAV vectors for gene thera...

Digital therapeutics and behavioral health company using software as medicine.

Biopharmaceutical company focused on drugs to treat CNS disorders by targeting neuronal nicotinic...

Private biopharmaceutical company focused on the development of therapies for retinal dystrophies.

Preclinical-stage biotech developing next-generation oncolytic virus therapies for solid tumors.

Orbis Medicines is pioneering a new era for oral macrocycle drug discovery.

Biotech developing antibody-based KnotBody therapeutics targeting ion channels and GPCRs to treat...

Oral pharmacological chaperone protein therapies to address diseases that result from protein mis...

A next-generation gene therapy company pioneering the development of targeted non-viral gene ther...

A clinical-stage oncology company advancing small molecules that combine both targeted and immune...

Clinical-stage biopharma developing topical nanoparticle therapies for eye diseases, including tr...

Cure Genetics is a Chinese biotech company developing AAV-based gene therapy vectors in partnersh...

Developing CRISPR-based therapies to cure viral infectious diseases.

Develops and commercializes neffy, an FDA-approved needle-free epinephrine nasal spray for treati...

Clinical-stage biotech developing immunotherapies that reprogram immune signaling to treat cancer...

Clinical-stage gene editing company developing in vivo therapies using its proprietary ARCUS geno...